Metagenomi says it hopes to start clinical trials next year to test MGX-001, its gene-editing therapy candidate for ...

For the first time in Denmark, people with hemophilia B have been treated with the gene therapy Hemgenix (etranacogene ...

Be Biopharma has raised $92 million to support the first-in-human Phase 1/2 trial of BE-101, which is made to lower bleeding ...

Columnist Jennifer Lynne, a veteran of Florida hurricanes, offers advice for those with bleeding disorders should evacuations be necessary.

Columnist Joe MacDonald reflects on how the Parents Empowering Parents program helped him and his wife manage their son's hemophilia.

Columnist G Shellye Horowitz explains why she joined a federal lawsuit against a California law requiring licensing for out-of-state doctors.

My husband, Jared, often spent his childhood navigating two very different worlds. In one, he was a regular kid with big dreams and boundless imagination. In the other, he was a young boy living with ...

Now that his adult sons are managing their own hemophilia care, columnist Joe MacDonald is able to consider moving for a job.

I don’t recall when I met Debbie Murray, but I remember the impression she left on me. Her frustration with the long and challenging journey to a proper diagnosis and effective treatment of her ...